Sanfilippo Syndrome Type A, also known as Mucopolysaccharidosis III A (MPS IIIA), is a rare, autosomal recessive lysosomal storage disorder. It is caused by a deficiency in the enzyme heparan-N-sulfatase, which is essential for breaking down heparan sulfate. The resulting accumulation of these sugar molecules leads to severe and progressive neurological degeneration, typically manifes... https://www.databridgemarketresearch.com/reports/global-sanfilippo-a-market